Status | Study |
Enrolling by invitation |
Study Name: Long-term Safety of Alpha1-Proteinase Inhibitor (Human) in Japanese Subjects With Alpha1 Antitrypsin Deficiency (GTI1401-OLE) Condition: Alpha1-Antitrypsin Deficiency Date: 2016-08-12 Interventions: Biological: Alpha-1 MP Weekly intravenous infusions of 60 mg/kg Alpha-1 MP |
Completed |
Study Name: Alpha-1 Carrier Genomics Study Condition: Alpha-1 Antitrypsin Deficiency Emphysema Date: 2016-06-20 Interventions: Genetic: Genetic Sequencing Sequencing of the SERPINA1 gene |
Enrolling by invitation |
Study Name: Long Term Safety of Alpha1-Proteinase Inhibitor in Subjects With Alpha1 Antitrypsin Deficiency Condition: Pulmonary Emphysema in Alpha-1 Antitrypsin Deficiency Date: 2016-06-03 Interventions: Biological: Alpha-1 MP Alpha-1 MP 60 mg/kg/week for up to 104 weeks |
Recruiting |
Study Name: Stage 1 Study of ARALAST NP and GLASSIA in A1PI Condition: Chronic Obstructive Pulmonary Disease Alpha1-antitrypsin Deficiency Date: 2016-03-23 Interventions: Biological: ARALAST NP 60 mg/kg |
Recruiting |
Study Name: Epigenetic Regulation of Immunity in Alpha-1 Anti-trypsin Deficiency Condition: Alpha 1-Antitrypsin Deficiency Date: 2016-02-12 |
Not yet recruiting |
Study Name: Microbioma in Sputa From COPD With Alpha-1 Antitrypsin Deficiency Condition: Alpha-1 Antitrypsin Deficiency Date: 2015-09-09 Interventions: Other: collection of sputum |
Recruiting |
Study Name: Ph 3/4 GLASSIA Safety, Immunogenicity, and Bronchoalveolar Lavage Study Condition: Alpha1-antitrypsin Deficiency Date: 2015-08-14 Interventions: Biological: GLASSIA 60 mg/kg BW administered at a rate of 0.2 mL/kg/min |
Active, not recruiting |
Study Name: A Study of an Investigational Drug, ALN-AAT, in Healthy Adult Subjects and Patients With ZZ Type Alpha-1 Antitrypsin Deficiency Liver Disease Condition: Antitrypsin Deficiency Liver Disease Date: 2015-07-16 Interventions: Drug: ALN-AAT Single or multip |
Recruiting |
Study Name: Environment Effect on Six-Minute Walk Test Performance Condition: Chronic Obstructive Pulmonary Disease Alpha-1 Antitrypsin Deficiency Date: 2015-06-09 Interventions: Other: six-minute walk study indoors |
Terminated |
Study Name: A Study of ARC-AAT in Healthy Volunteer Subjects and Patients With Alpha-1 Antitrypsin Deficiency (AATD) Condition: Alpha-1 Antitrypsin Deficiency Date: 2015-02-02 Interventions: Drug: ARC-AAT Injection RNA in |